Clinical Effects of Oral Trehalose In Patients With Spinocerebellar Ataxia 3
Clinical Effects of Oral Trehalose In Patients With Spinocerebellar Ataxia 3
NCT ID: NCT04426149 Phase: NA Status: COMPLETED Enrollment: 13 Completion: 2018-09-07
Conditions
Spinocerebellar Ataxia 3
Interventions
trehalose
Summary
There are no clinically established treatments which have been proven to delay the disease progression in spinocerebellar ataxia (SCA) 3. Most available treatments are only for symptom alleviation, and thus the majority of patients will eventually progress to needing and wheel chair and eventually bedridden.
As trehalose appear to be potentially promising treatment in SCA, the investigators aim to conduct this study using oral trehalose in our genetically confirmed SCA 3 patients.
Primary Outcome
scale of rating of ataxia (SARA) score months,